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Autori: Mengel Eugen

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Naslov A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase (Article)
Autori Pastores Gregory M Petakov Milan S Giraldo Pilar Rosenbaum Hanna Szer Jeffrey Deegan Patrick B Amato Dominick J Mengel Eugen Tan Ee Shien Chertkoff Raul Brill-Almon Einat Zimran Ari 
Info BLOOD CELLS MOLECULES AND DISEASES, (2014), vol. 53 br. 4, str. 253-260
Projekat Protalix BioTherapeutics; Pfizer
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science   Scopus  
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Naslov Peripheral neuropathy in adult type 1 Gaucher disease: a 2-year prospective observational study (Article)
Autori Biegstraaten Marieke Mengel Eugen Marodi Laszlo Petakov Milan S Niederau Claus Giraldo Pilar Hughes Derralyn Mrsic Mirando Mehta Atul Hollak Carla EM van Schaik Ivo N 
Info BRAIN, (2010), vol. 133 br. , str. 2909-2919
Projekat European Working Group on Gaucher Disease (EWGGD) ; Actelion Pharmaceuticals Ltd ; Actelion Pharmaceuticals Ltd, Allschwil, Switzerland
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science   Scopus  
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